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Gene Therapy

Gene therapies are redefining the treatment of rare diseases. However, a set of complex and unique challenges must be overcome for these therapeutics to achieve their commercial potential.

The Gene Therapy for Rare Disorders event series is dedicated to addressing the latest clinical, manufacturing, regulatory and commercialization challenges facing this field, enabling you to deliver on the promise of gene therapies.


“This is "the conference" to attend for professionals that are already involved or about to embark in the gene therapy space””
Bill White, Senior Director, Market Access, AveXis